FDA Approves INCIVEK

FDA Approves INCIVEK™ (telaprevir) for People with Hepatitis C

-79% of people treated for the first time achieved a SVR (viral cure)

with INCIVEK combination treatment-

-Vertex launches a comprehensive financial assistance and patient

support program-

-Conference call today at 11:00 a.m. ET to provide more information

on the commercialization of INCIVEK-

CAMBRIDGE, Mass.–(BUSINESS WIRE)–

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced that

the U.S. Food and Drug Administration (FDA) has approved INCIVEK™

(telaprevir) tablets for a broad group of people with genotype 1 chronic

hepatitis C with compensated liver disease (some level of damage to the

liver but the liver still functions), including cirrhosis (scarring of

the liver). INCIVEK (in-SEE-veck) is approved for people who are new to

treatment, and for people who were treated previously but who did not

achieve a viral cure (relapsers, partial responders and null

responders). INCIVEK is given for 12 weeks in combination with

pegylated-interferon and ribavirin, two other medicines approved to

treat hepatitis C. After the first 12 weeks, all patients stop receiving

INCIVEK and continue treatment with pegylated-interferon and ribavirin

alone for an additional 12 weeks or 36 weeks of treatment. With INCIVEK

combination treatment, more than 60 percent of people treated for the

first time, as well as those who relapsed after previous therapy, are

expected to complete all treatment in 24 weeks — half the time needed if

they were to take pegylated-interferon and ribavirin alone. All other

patients will receive a total of 48 weeks of treatment. INCIVEK will

arrive in pharmacies this week.

INCIVEK (750 mg) is given as two 375-mg tablets three times daily for 12 weeks. It is packaged in we ...

INCIVEK (750 mg) is given as two 375-mg tablets three times daily for 12 weeks. It is packaged in weekly boxes that include daily blister strips to help patients keep track of their doses. (Photo: Business Wire)

The approval of INCIVEK was based on data from three Phase 3 studies,

which showed that people who received INCIVEK combination treatment

achieved significantly higher rates of sustained viral response (SVR, or

viral cure) compared to those who received pegylated-interferon and

ribavirin alone, regardless of their prior treatment experience:

 

 

People new to treatment:

79 percent vs. 46 percent

 

People who were treated previously but did not achieve a viral

cure:

– Relapsers:

86 percent vs. 22 percent

– Partial responders:

59 percent vs. 15 percent

– Null responders:

32 percent vs. 5 percent

 

INCIVEK (750 mg) is given as two 375-mg tablets three times daily. It is

packaged in weekly boxes that include daily blister strips to help

patients keep track of their doses.

Rash and anemia are the most serious side effects associated with

INCIVEK. The most common side effects reported with INCIVEK combination

treatment include fatigue, itching, nausea, diarrhea, vomiting, anal or

rectal problems, and taste changes.

“Hepatitis C can lead to liver failure, cancer and the need for a

transplant, and for the past decade, the best we could offer patients

was a year of difficult treatment that resulted in a viral cure for

fewer than half of them,” said Ira Jacobson, M.D., Chief of the Division

of Gastroenterology and Hepatology, Weill Cornell Medical College and

principal investigator for a Phase 3 study of INCIVEK. “With INCIVEK, 79

percent of people new to treatment achieved a viral cure.”

“Today marks a turning point in the fight against hepatitis C,

particularly for people who have been living with this silent disease

for decades, hoping for a better chance of a viral cure,” said Matthew

Emmens, Chairman, President and Chief Executive Officer of Vertex. “The

approval of INCIVEK was only possible thanks to more than 4,000 people

who volunteered for our clinical studies, the doctors, nurses and

coordinators who managed the studies, and our own pioneering scientists

who have worked for more than 15 years to bring this new medicine to

people with hepatitis C.”

Vertex has 200 field-based employees across the United States, including

a 115-person sales team, who are ready to support the introduction of

INCIVEK. The sales team has an average of more than 14 years of

experience bringing medicines to people who need them, including eight

years of direct experience with antiviral medicines for diseases such as

hepatitis C.

Helping People with Hepatitis C Get INCIVEK

The people who work at Vertex understand that medicines can only help

patients who can get them. With that in mind, the company today

introduced a comprehensive financial assistance and patient support

program to help people get INCIVEK who might not otherwise be able to

afford it. The program will help people with hepatitis C learn about

insurance benefits for their medicines, give INCIVEK for free to

eligible patients who do not have insurance and provide coverage for

co-pay or co-insurance costs associated with INCIVEK for people who meet

certain program criteria. Additionally, patients will have access to

nurses through a 24-7 hotline by which they can receive support,

guidance and educational materials about hepatitis C and its treatment.

Vertex will also provide nurses and doctors with educational tools and

resources so they can offer support and care to people with hepatitis C

before, during and after the treatment process.

For eligible patients, the program includes the following:

  • Insurance Benefits Research and Support: Vertex case managers will

    research patients’ insurance benefits for INCIVEK combination

    treatment, assist people with insurance appeals and help guide them to

    other forms of financial support, including Vertex’s free medicine and

    co-pay programs;

  • Free Medicine Program: Vertex will give INCIVEK for free to people who

    do not have insurance and have an annual household income of $100,000

    or less; and

  • Co-Pay Support: Vertex will cover co-pay or co-insurance costs up to

    20 percent of the total cost of INCIVEK for people who have private

    insurance plans that cover INCIVEK, regardless of their household

    income. For people covered by government insurance, Vertex will also

    make donations to the independent, non-profit Patient Access Network

    Foundation, which has a fund to provide co-pay support to people

    taking hepatitis C medicines.

More information about this program is available by calling

1-855-837-8394 or visiting www.INCIVEK.com.

About INCIVEK

INCIVEK is an oral medicine that acts directly on the hepatitis C virus

protease, an enzyme essential for viral replication. The Phase 3

registration studies evaluated INCIVEK in combination with Pegasys®

(pegylated-interferon alfa-2a) and Copegus® (ribavirin) in

people with hepatitis C who were new to treatment as well as those who

were treated previously with pegylated-interferon and ribavirin but who

did not achieve a viral cure, including:

  • Prior Relapsers: Defined as people whose

    hepatitis C virus was undetectable after a full course of previous

    treatment, but whose virus became detectable during the follow-up

    period;

  • Prior Partial Responders: Defined as

    people who achieved at least a 2 log10 reduction in

    hepatitis C virus at week 12, but whose hepatitis C virus never became

    undetectable by week 24 of a prior course of therapy; and

  • Prior Null Responders: Defined as people

    who achieved a less than 2 log10 reduction in hepatitis C

    virus at week 12 of a prior course of therapy.

Vertex developed telaprevir in collaboration with Tibotec BVBA and

Mitsubishi Tanabe Pharma. Vertex has rights to commercialize telaprevir

in North America. Through its affiliate, Janssen, Tibotec has rights to

commercialize telaprevir in Europe, South America, Australia, the Middle

East and certain other countries. Mitsubishi Tanabe Pharma has rights to

commercialize telaprevir in Japan and certain Far East countries. In the

United States, telaprevir will be marketed with the brand name INCIVEK.

Indication

INCIVEK™ (telaprevir) is a prescription medicine used with the medicines

peginterferon alfa and ribavirin to treat chronic (lasting a long time)

hepatitis C genotype 1 infection in adults with stable liver problems,

who have not been treated before or who have failed previous treatment.

It is not known if INCIVEK is safe and effective in children under 18

years of age.

IMPORTANT SAFETY INFORMATION

Who should not take INCIVEK?

Do not take INCIVEK if you are pregnant or may become pregnant,

or if you are a man with a sexual partner who is pregnant.

Do not take INCIVEK if you are taking certain medicines as there could

be serious side effects. If these drugs are taken together, this can

cause you to have too much or not enough INCIVEK or your other medicines

in your body. It can also cause side effects that can be serious or

life-threatening. These medicines include: alfuzosin hydrochloride

(Uroxatral®), atorvastatin (Lipitor®, Caduet®),

ergot containing medicines such as methylergonovine (Methergine®),

lovastatin (Advicor®, Altoprev®, Mevacor®),

pimozide (Orap®), rifampin (Rifadin®, Rifamate®,

Rifater®), sildenafil citrate (Revatio®) or

tadalafil (Adcirca®) for the lung problem pulmonary artery

hypertension (PAH), simvastatin (Zocor®, Vytorin®,

Simcor®), St. John’s wort (Hypericum perforatum), or

triazolam (Halcion®).

Talk to your healthcare provider before taking INCIVEK if any of the

above applies to you. Your healthcare provider may need to change the

amount of medicines you take.

Tell your healthcare provider about all the medicines you take,

including prescription and non-prescription medicines, vitamins, and

herbal supplements. INCIVEK and other medicines can affect each other.

Serious Side Effects

INCIVEK can cause serious side effects, including:

  • Birth defects or death of an unborn baby
    INCIVEK combined with

    peginterferon alfa and ribavirin may cause birth defects or death of

    your unborn baby. If you or your sexual partner is pregnant or plan to

    become pregnant, do not take these medicines. You or your partner

    should not become pregnant while taking INCIVEK with peginterferon

    alfa and ribavirin and for 6 months after treatment is over.

    You

    must have a negative pregnancy test before starting treatment, every

    month during treatment, and for 6 months after your treatment ends.

    You must use 2 effective methods of birth control during treatment and

    for 6 months after all treatment has ended. These 2 forms of birth

    control should not contain hormones, as these may not work as well

    during treatment with INCIVEK. Talk to your healthcare provider about

    the forms of birth control you should use during this time.

    Two

    weeks after stopping INCIVEK, you can use a hormonal form of birth

    control as one of your two forms of birth control.

    If you

    or your partner becomes pregnant during treatment or within 6 months

    after stopping these medicines, tell your healthcare provider right

    away. Contact the Ribavirin Pregnancy Registry right away by calling

    1-800-593-2214. The Registry collects information about what happens

    to mothers and their babies if the mother takes ribavirin while

    pregnant.

  • Skin reactions: Mild skin rashes are common with INCIVEK combination

    treatment. Sometimes these skin rashes and other skin reactions can

    become severe and require treatment in a hospital.

    Call

    your healthcare provider right away if you develop any skin changes

    with these symptoms: rash with or without itching, blisters or skin

    lesions, mouth sores or ulcers, red or inflamed eyes like “pink eye”

    (conjunctivitis), swelling of your face, or fever.

    Your

    healthcare provider will decide if these changes may be a sign of a

    serious skin reaction. Your healthcare provider will also decide if

    you need treatment for your rash or to stop INCIVEK or your other

    medicines. Never stop taking INCIVEK combination treatment without

    talking to your healthcare provider first.

  • Do not take INCIVEK alone to treat chronic hepatitis C infection. It

    must be used with peginterferon alfa and ribavirin to treat chronic

    hepatitis C infection.

  • Low red blood cell count (anemia) that can be severe. Tell your

    healthcare provider if you have any of these symptoms of anemia:

    dizziness, shortness of breath, tiredness, or weakness.

    Your

    healthcare provider will do blood tests regularly to check your red

    blood cell count during treatment. If your anemia is severe your

    healthcare provider may tell you to stop taking INCIVEK. If this

    happens, do not start taking it again.

What should I tell my healthcare provider before taking INCIVEK?

Tell your healthcare provider if you:

  • have certain blood problems such as anemia

  • have liver problems other than hepatitis C infection

  • have hepatitis B, HIV infection, or any problems with your immune

    system

  • have a history of gout or high uric acid levels in your blood

  • have had an organ transplant

  • plan to have surgery

  • have any other medical condition

  • are breastfeeding

How should I take INCIVEK?

Take INCIVEK exactly as your healthcare provider tells you. Take 2

INCIVEK pills 3 times a day, 7 to 9 hours apart, with food. Eat a meal

or snack containing about 20 grams of fat within 30 minutes before you

take each dose. Talk to your healthcare provider about examples of food

you can eat.

If you miss a dose within 4 hours of when you usually take it, take your

dose with food as soon as possible. If you miss a dose and it is more

than 4 hours after the time you usually take it, skip that dose only and

take the next dose at your normal time. Do not stop taking INCIVEK

unless your healthcare provider tells you to. If your healthcare

provider tells you to stop, you should not start taking it again, even

if the reason for stopping goes away. If you take too much INCIVEK, call

your healthcare provider or local Poison Control Center, or go to the

nearest emergency room right away.

Common Side Effects of INCIVEK Combination Treatment

The most common side effects include itching, nausea, diarrhea,

vomiting, anal or rectal problems (including hemorrhoids, discomfort or

burning around or near the anus, itching around or near the anus), taste

changes, and tiredness. Tell your healthcare provider about any side

effect that bothers you or doesn’t go away.

These are not all the possible side effects of INCIVEK. For more

information, ask your healthcare provider or pharmacist.

You are encouraged to report negative side effects of prescription drugs

to the FDA at 1-800-FDA-1088 or 1-800-332-1088 or www.fda.gov/medwatch.

You may also report side effects to Vertex Pharmaceuticals Incorporated

at 1-877-824-4281.

Please see full Prescribing Information for INCIVEK including the

Medication Guide available at www.INCIVEK.com.

For healthcare providers who are interested in information about

INCIVEK, you can also call 1-877-824-4281.

Conference Call Information

Vertex will host a conference call and webcast today, May, 23, 2011 at

11:00 a.m. ET to provide more information about today’s approval, the

price of INCIVEK and Vertex’s new financial assistance and patient

support program. The conference call will be webcast live and a link to

the webcast may be accessed from the ‘Events & Presentations’ page of

Vertex’s website at www.vrtx.com.

To listen to the call on the telephone, dial 1-866-501-1537 (United

States and Canada) or 1-720-545-0001 (International). Vertex is also

providing a podcast MP3 file available for download on the Vertex

website at www.vrtx.com.

The conference ID number for the live call and replay is 68267164. The

call will be available for replay via telephone commencing May 23, 2011

at 5:00 p.m. ET running through 5:00 p.m. ET on May 30, 2011. The replay

phone number for the United States and Canada is 1-800-642-1687. The

international replay number is 1-706-645-9291. Following the live

webcast, an archived version will be available on Vertex’s website until

5:00 p.m. ET on June 6, 2011. To ensure a timely connection, it is

recommended that users register at least 15 minutes prior to the

scheduled webcast.

INCIVEK™ is a trademark of Vertex Pharmaceuticals Incorporated.

PEGASYS® and COPEGUS® are registered trademarks of

Hoffmann-La Roche.

About Hepatitis C

Hepatitis C is a serious liver disease caused by the hepatitis C virus,

which is spread through direct contact with the blood of infected people

and ultimately affects the liver.1 Chronic hepatitis C can

lead to serious and life-threatening liver problems, including liver

damage, cirrhosis, liver failure or liver cancer.1 Though

many people with hepatitis C may not experience symptoms, others may

have symptoms such as fatigue, fever, jaundice and abdominal pain.1

Unlike HIV and hepatitis B virus, chronic hepatitis C is curable.2

However, approximately 60 percent of people do not achieve SVR,3,4,5

or viral cure,6 after treatment with 48 weeks of

pegylated-interferon and ribavirin alone. If treatment is not successful

and a person does not achieve a viral cure, they remain at an increased

risk for progressive liver disease.7,8

More than 170 million people worldwide are chronically infected with

hepatitis C.6 In the United States, nearly 4 million people

have chronic hepatitis C and 75 percent of them are unaware of their

infection.9 Hepatitis C is four times more prevalent in the

United States compared to HIV.9 The majority of people with

hepatitis C in the United States were born between 1946 and 1964,

accounting for two of every three people with chronic hepatitis C.10

Hepatitis C is the leading cause of liver transplantations in the United

States and is reported to contribute to 4,600 to 12,000 deaths annually.11,12

By 2029, total annual medical costs in the United States for

people with hepatitis C are expected to more than double, from $30

billion in 2009 to approximately $85 billion.9

About Vertex

Vertex creates new possibilities in medicine. Our team discovers,

develops and commercializes innovative therapies so people with serious

diseases can lead better lives. Vertex scientists and our collaborators

are working on new medicines to cure or significantly advance the

treatment of hepatitis C, cystic fibrosis, epilepsy and other

life-threatening diseases.

Founded more than 20 years ago in Cambridge, MA, we now have ongoing

worldwide research programs and sites in the U.S., U.K. and Canada.

Special Note Regarding Forward-Looking Statements

This press release contains forward-looking statements, as defined in

the Private Securities Litigation Reform Act of 1995, as amended,

including statements regarding (i) Vertex’s sales team being ready to

support the introduction of INCIVEK, (ii) Vertex’s financial assistance

and patient support programs and its commitment to help people who might

not otherwise be able to afford INCIVEK receive it and (iii) the use of

INCIVEK as a treatment for people with genotype 1 chronic hepatitis C

virus infection. While the company believes the forward-looking

statements contained in this press release are accurate, there are a

number of factors that could cause actual events or results to differ

materially from those indicated by such forward-looking statements.

Those risks and uncertainties include, among other things, risks related

to the commercialization of INCIVEK and the other risks listed under

Risk Factors in Vertex’s annual report and quarterly reports filed with

the Securities and Exchange Commission and available through Vertex’s

website at www.vrtx.com.

Vertex disclaims any obligation to update the information contained in

this press release as new information becomes available.

For more information and to view Vertex’s press releases, please visit www.vrtx.com.

(VRTX – GEN)

1 Centers for Disease Control and Prevention. Hepatitis C

Fact Sheet: CDC Viral Hepatitis. Available at: http://www.cdc.gov/hepatitis/HCV/PDFs/HepCGeneralFactSheet.pdf.

Accessed March 21, 2011.
2 Pearlman BL and Traub N.

Sustained Virologic Response to Antiviral Therapy for Chronic Hepatitis

C Virus Infection: A Cure and So Much More. Clin Infect Dis. 2011

Apr;52(7):889-900.
3 Manns MP, McHutchison JG, Gordon

SC, et al. Peginterferon alfa-2b plus ribavirin compared with interferon

alfa-2b plus ribavirin for initial treatment of chronic hepatitis C: a

randomised trial. Lancet. 2001;358:958-965.
4

Fried MW, Shiffman ML, Reddy KR, et al. Peginterferon alfa-2a plus

ribavirin for chronic hepatitis C virus infection. N Engl J Med.

2002;347:975-982.
5 McHutchison JG, Lawitz EJ, Shiffman

ML, et al; IDEAL Study Team. Peginterferon alfa-2b or alfa-2a with

ribavirin for treatment of hepatitis C infection. N Engl J Med.

2009;361:580-593.
6 Ghany MG, Strader DB, Thomas DL,

Seeff, LB. Diagnosis, management and treatment of hepatitis C; An

update. Hepatology. 2009;49 (4):1-40.
7 Morgan

TR, Ghany MG, Kim HY, Snow KK, Lindsay K, Lok AS. Outcome of sustained

virological responders and non-responders in the Hepatitis C Antiviral

Long-Term Treatment Against Cirrhosis (HALT-C) trial. Hepatology.

2008;50(Suppl 4):357A (Abstract 115).
8 Veldt BJ,

Heathcote J, Wedmeyer H. Sustained virologic response and clinical

outcomes in patients with chronic hepatitis C and advanced fibrosis.

Annals of Internal Medicine. 2007; 147: 677-684.
9

Institute of Medicine of the National Academies. Hepatitis and liver

cancer: a national strategy for prevention and control of hepatitis B

and C. Colvin HM and Mitchell AE, ed. Available at: http://www.iom.edu/Reports/2010/Hepatitis-and-Liver-Cancer-A-National-Strategy-for-Prevention-and-Control-of-Hepatitis-B-and-C.aspx.

Updated January 11, 2010. Accessed March 21, 2011.
10

Pyenson B, Fitch K, Iwasaki K. Consequences of hepatitis C virus (HCV):

Costs of a baby boomer epidemic of liver disease. Available at: http://www.natap.org/2009/HCV/051809_01.htm.

Updated May 2009. Accessed March 21, 2011. This report was

commissioned by Vertex Pharmaceuticals, Inc.
11 Volk

MI, Tocco R, Saini S, Lok, ASF. Public health impact of antiviral

therapy for hepatitis C in the United States. Hepatology.

2009;50(6):1750-1755.
12 Davis GL, Alter MJ, El-Serag H,

Poynard T, Jennings LW. Aging of hepatitis C virus (HCV)-infected

persons in the United States: A multiple cohort model of HCV prevalence

and disease progression. Gastroenterology. 2010;138:513-521.

Photos/Multimedia Gallery Available: http://www.businesswire.com/cgi-bin/mmg.cgi?eid=6733469〈=en

Vertex::
Media: Dawn Kalmar Amy Pasqua Zachry

Barber617-444-6992 or mediainfo@vrtx.com
or
Investors: Michael

Partridge, 617-444-6108
Lora Pike, 617-444-6755 Matthew

Osborne, 617-444-6057

Source: Vertex Pharmaceuticals Incorporated

News Provided by Acquire Media

Leave a Reply

Your email address will not be published. Required fields are marked *

*

You may use these HTML tags and attributes: <a href="" title=""> <abbr title=""> <acronym title=""> <b> <blockquote cite=""> <cite> <code> <del datetime=""> <em> <i> <q cite=""> <strike> <strong>